Delaware Newborn Screening
Metabolic Disorders
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TRADITIONAL DISORDERS
- CH – Congenital Hypothyroidism
- CAH – Congenital Adrenal Hyperplasia
- GAL – Galactosemia
- HGB – Hemoglobinopathies – SS Disease, SC Disease, Variant Hgb
- BIOT – Biotinidase Deficiency
- CF – Cystic Fibrosis
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AMINO ACID/UREA CYCLE DISORDERS (MS/MS)
- PKU – Phenylketonuria
- HPHE – Hyperphenylalanemia
- MSUD – Maple Syrup Urine Disease
- HCYS – Homocystinuria
- HMET – Hypermethioninemia
- TYR – Tyrosinemia, Type I
- TYR – Tyrosinemia, Type II
- TYR – Tyrosinemia, Type III
- ARG – Argininemia
- ASL – Argininosuccinate Lyase Deficiency
- CIT – Argininosuccinate Synthetase Deficiency (Citrullinemia)
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ORGANIC ACID DISORDERS (MS/MS)
- GA-1 – Glutaric Acidemia, Type I
- PA – Proprionic Acidemia
- MMA – Methylmalonic Acidemia
- MCD – Multiple Carboxylase Deficiency
- IVA – Isovaleric Acidemia
- 2-MBCD – 2-Methylbutyryl-CoA Dehydrogenase Deficiency
- 3-MCC – 3-Methylcrotonyl-CoA Carboxylase Deficiency
- HMG – 3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency
- BKT – Mitochondrial Acetoacetyl-CoA Thiolase Deficiency
- IBCD – Isobutyryl-CoA Dehydrogenase Deficiency
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FATTY ACID OXIDATION DISORDERS (MS/MS)
- MCAD – Medium Chain Acyl-CoA Dehydrogenase Deficiency
- CPT II – Carnitine Palmitoyltransferase II Deficiency
- CAT – Carnitine/Acylcarnitine Translocase Deficiency
- GA II – Glutaric Acidemia, Type II
- MADD – Multiple Acyl-CoA Dehydrogenase Deficiency
- SCAD – Short-Chain Acyl-CoA Dehydrogenase Deficiency
- LCHAD – Long-Chain Hydroxyacyl-CoA Dehydrogenase Deficiency
- TFP – Trifunctional Protein Deficiency
- VLCAD – Very Long-Chain Acyl-CoA Dehydrogenase Deficiency
- CUD – Carnitine Uptake Deficiency
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OTHER
- NH – Newborn Hearing Screening
- SCID – Severe Combined Immunodeficiency
- CCHD – Critical Congenital Heart Disease (January 2013)
- MPS-I – Mucopolysaccharidosis Type I
- Pompe – Glycogen Storage Disease Type II
- X-ALD – X-linked Adrenoleukodystrophy
- SMA – Spinal Muscular Atrophy
Disorder | Frequency |
---|---|
Phenylketonuria (PKU) | 1:15,000 |
Congenital Hypothyroidism (CH) | 1:4,000 |
Galactosemia | 1:45,000 |
Hemoglobinopathies | 1:400 (African Ancestory) |
Congenital Adrenal Hyperplasia (CAH) | 1:12,000 |
Medium Chain Acyl CO-A Dehydrogenase Deficiency (MCAD) | 1:15,000 |
Other Fatty Acid Oxidation (FAO) Disorders | 1:15,000 |
Maple Syrup Urine Disease (MSUD) | 1:40,000 |
Homocystinuria | 1:70,000 |
Certain other disorders of amino acid metabolism (not including Ornithine Transcarbamylase Deficiency (OTC) 1 | 1:20,000 |
Glutaric Aciduria 1 | 1:100,000 (higher in Amish) |
Other Organic Acid Disorders | 1:20,000 |
Biotinidase Deficiency | 1:60,000 |
Severe Combined Immunodeficiency (SCID) | 1:100,000 |
Mucopolysaccharidosis Type I (MPS-I) | 1:100,000 |
Glycogen Storage Disease Type II (Pompe) | 1:40,000 |
X-linked Adrenoleukodystrophy (X-ALD) | 1:50,000 |
Spinal Muscular Atrophy (SMA) | 1:10,000 |